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Coordinated β-globin expression and α2-globin reduction in a multiplex  lentiviral gene therapy vector for β-thalassemia: Molecular Therapy
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy

Current status of beta‐thalassemia and its treatment strategies - Ali -  2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library

JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging  Treatments for Thalassemia?
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?

Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A  Panoramic Review
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review

Β-Thalassemias | NEJM
Β-Thalassemias | NEJM

Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the  Horizon | Article
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon | Article

β-Thalassemia | Genetics in Medicine
β-Thalassemia | Genetics in Medicine

Thalassaemia - The Lancet
Thalassaemia - The Lancet

Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising  One-Time Therapeutic Approach for Transfusion-Dependent  β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia
Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia

Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron  Chelation | SpringerLink
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink

IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?
IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?

Cure for thalassemia major – from allogeneic hematopoietic stem cell  transplantation to gene therapy | Haematologica
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica

Full article: Revisiting beta thalassemia intermedia: past, present, and  future prospects
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects

Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th  Edition - Version 2.0) by Thalassaemia International Federation (TIF) -  Issuu
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu

Β-Thalassemias | NEJM
Β-Thalassemias | NEJM

Cure for thalassemia major – from allogeneic hematopoietic stem cell  transplantation to gene therapy | Haematologica
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica

Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of  Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary  Myelofibrosis
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis

Replacing the suppressed hormone: toward a better treatment for iron  overload in β-thalassemia major? | Haematologica
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica

Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article

Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering  the Expression of α-Globin Gene
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene

Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)

Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)

PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making  Algorithm
PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm

Luspatercept for the treatment of β-thalassemia: from preclinical research  to clinical practice and beyond | Future Rare Diseases
Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases

Significance of genetic modifiers of hemoglobinopathies leading towards  precision medicine | Scientific Reports
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports